Australia's most trusted
source of pharma news
Friday, 05 December 2025
Posted 5 December 2025 AM
The TGA is reviewing what could become one the most expensive treatments in Australia - a new form of Novartis' gene therapy Zolgensma, which carries a price tag of $4 million for a one-time dose.
And in what could be a good sign, the treatment for spinal muscular atrophy (SMA) was recently approved by the FDA for the same indication currently under TGA consideration, which includes a different cohort of patients than those covered by the current PBS listing.

Please click the button to indicate that the printout of this article is for your personal use only and not for any type of redistribution.
Redistribution of the whole or part of Pharma in Focus by any means is a breach of copyright law.